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Pioneering a new class of RNA medicines to increase targeted gene expression

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The Problem

Inadequate gene expression is the underlying cause of more than a thousand diseases

Our Solution

ASO therapeutics designed to selectively upregulate gene expression by modulating regulatory RNA and directly address the underlying cause of protein deficiency with precision and control.

Discover Our Scientific Approach

About Us

Led by an experienced leadership team with deep expertise in RNA biology and drug development.

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  • person presenting on a stage in an auditorium. part of a slide with a scientific graphic is visible above him.
  • 2 tema members posing in front of a wall with the ASGCT logo painted
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  • CAMP4's president smiling in a suit in front of an abstract background
  • Yuri Maricich presenting at a podium, next to a slide with his name on it
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Pipeline

We are advancing a pipeline of first-in-class ASO-based therapeutics with the potential to address diseases characterized by insufficient protein expression.

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Williams Family, AUS

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Disease Areas

We aim to bring life-changing therapies to patient communities with limited to no treatment options.

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Investors

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